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Our Patients
Our Promise to Patients: You Come First
Welcome
Our activities are based on our promise to save lives and to improve the lives of our patients and their families, as living with a rare disease impacts more than just one person. We offer self-help programmes and activities, and work with patient organisations to improve educational activities and raise public awareness. In addition, we work hand in hand with the healthcare authorities to ensure that patients have access to the medicines they need to help them lead a full life.